0 Yorumlar
0 hisse senetleri
129 Views
0 önizleme
Site içinde arama yapın
Yeni insanlarla keşfedin, yeni bağlantılar oluşturmak ve yeni arkadaşlar edinmek
-
Please log in to like, share and comment!
-
Exon-Skipping and Beyond: Tracking the Evolving Standard of Care and Pipeline Dynamics in the Multi-Billion Dollar Duchenne Muscular Dystrophy Market.The Duchenne Muscular Dystrophy (DMD) standard of care has been fundamentally altered by the introduction of exon-skipping oligonucleotide therapies. These drugs work by coaxing the cell's machinery to "skip" over a specific defective exon in the dystrophin gene, allowing the production of a truncated, but partially functional, dystrophin protein. While only applicable to specific genetic...0 Yorumlar 0 hisse senetleri 179 Views 0 önizleme